Nusinersen in infants who initiate treatment in a presymptomatic stage of spinal muscular atrophy: interim results from the phase 2 NURTURE study

Ryan M., De Vivo D., Bertini E., Hwu W., Crawford T., Swoboda K., ...More

24th International Annual Congress of the World-Muscle-Society (WMS), Copenhagen, Denmark, 1 - 05 October 2019, vol.29 identifier

  • Publication Type: Conference Paper / Summary Text
  • Volume: 29
  • Doi Number: 10.1016/j.nmd.2019.06.518
  • City: Copenhagen
  • Country: Denmark
  • Hacettepe University Affiliated: Yes