Efficacy and safety results of the avalglucosidase alfa phase 3 COMET trial in late-onset Pompe disease patients

Kishnani P. S., Attarian S., Borges J. L., Bouhourd F., Chien Y., Choi Y., ...More

MOLECULAR GENETICS AND METABOLISM, vol.132, no.2, 2021 (SCI-Expanded) identifier

  • Publication Type: Article / Abstract
  • Volume: 132 Issue: 2
  • Publication Date: 2021
  • Doi Number: 10.1016/j.ymgme.2020.12.127
  • Journal Name: MOLECULAR GENETICS AND METABOLISM
  • Journal Indexes: Science Citation Index Expanded (SCI-EXPANDED), Scopus, Academic Search Premier, BIOSIS, CAB Abstracts, Chemical Abstracts Core, EMBASE, MEDLINE, Veterinary Science Database
  • Hacettepe University Affiliated: Yes