Allele-Specific Antisense Oligonucleotides for the Treatment of BEST1-Related Dominantly Inherited Retinal Diseases: An In Vitro Model
EUROPEAN JOURNAL OF HUMAN GENETICS, pp.1795, 2024 (SCI-Expanded, Scopus)
- Publication Type: Article / Abstract
- Publication Date: 2024
- Journal Name: EUROPEAN JOURNAL OF HUMAN GENETICS
- Journal Indexes: Science Citation Index Expanded (SCI-EXPANDED), Scopus, Academic Search Premier, BIOSIS, CAB Abstracts, EMBASE, MEDLINE, Veterinary Science Database
- Page Numbers: pp.1795
- Hacettepe University Affiliated: Yes