The avalglucosidase alfa phase 3 COMET trial in late-onset Pompe disease patients: Efficacy and safety results after 97 weeks

Kishnani P., Diaz-Manera J., Kushlaf H., Ladha S., Mozaffar T., Straub V., ...Daha Fazla

MOLECULAR GENETICS AND METABOLISM, cilt.135, sa.2, 2022 (SCI-Expanded) identifier

  • Yayın Türü: Makale / Özet
  • Cilt numarası: 135 Sayı: 2
  • Basım Tarihi: 2022
  • Doi Numarası: 10.1016/j.ymgme.2021.11.168
  • Dergi Adı: MOLECULAR GENETICS AND METABOLISM
  • Derginin Tarandığı İndeksler: Science Citation Index Expanded (SCI-EXPANDED), Scopus, Academic Search Premier, BIOSIS, CAB Abstracts, Chemical Abstracts Core, EMBASE, MEDLINE, Veterinary Science Database
  • Hacettepe Üniversitesi Adresli: Evet