Safety and Efficacy of Liver-Directed Gene Therapy in Patients with Mucopolysaccharidosis Type VI

Brunetti-Pierri N., Ferla R., Ginocchio V. M. , Rossi A., Fecarotta S., Romano R., ...More

MOLECULAR THERAPY, vol.29, no.4, pp.114, 2021 (Journal Indexed in SCI) identifier

  • Publication Type: Article / Abstract
  • Volume: 29 Issue: 4
  • Publication Date: 2021
  • Title of Journal : MOLECULAR THERAPY
  • Page Numbers: pp.114